Gene therapy for haemophilia B in the UK? Hold your horses!

After years on the track, gene therapy for haemophilia seems to have the home straights firmly in sight. Products for haemophilia A (Roctavian) and haemophilia B (Hemgenix) are licensed in Europe and the United States, and the first commercial doses have now been given. The remaining hurdles, however, are considerable: funding, reimbursement, and commissioning. In …

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